A Champaign second-grader hopes her family's fundraiser can help a kid in the future have a more "normal" childhood, not ...

A well-connected drug company and Laura Loomer wanted Kennedy ally Vinay Prasad gone. Trump chief of staff Susie Wiles got ...

Among a clutch of trailblazers at the forefront of the game in the north during the late Noughties, Marc helped break down the barriers to greater facilities and funding – not just through the spirit ...

The Health Resources and Services Administration is requesting public comments on its recommendation to add metachromatic ...

Arrowhead Pharmaceuticals stock tumbled Thursday after Sarepta Therapeutics liquefied its entire stake in the smaller biotech ...

The family of a child with Duchenne are considering legal action against the health service for denying access to a drug ...

Liquidating its stake in Arrowhead helps Sarepta cover a milestone payment and secure what one analyst described as ...

After two patients who received the investigational CDC7 blocker died, pushing forward with SGR-2921’s development would be ...

Agamree, an approved steroid treatment for Duchenne MD, will be sold in Turkey by GEN, per an agreement with Santhera.