Lizzy Lawrence leads STAT’s coverage of the Food and Drug Administration. She was previously a medical devices reporter. You can reach Lizzy on Signal at lizzylaw.53. John Wilkerson is a Washington ...
The Food and Drug Administration (FDA) announced a new proposal Monday for flexible drug approval pathway treatments addressing ultrarare diseases. The FDA unveiled draft guidance on a proposed ...
A genetics‑guided small molecule called compound 6 gently turns down an overactive immune pathway (CARD9), offering a more precise, durable, and potentially safer treatment strategy for Crohn’s ...
Feb 5 (Reuters) - (This Feb 5 story has been corrected to fix Prolia's 2025 sales to $4.4 billion, not $1.05 billion, in paragraph 5) Sign up here. Its pharmacy benefit management unit, Caremark, will ...
'Defying Rare Disease' premieres Thursday at 7 p.m. ET Susannah Rosen was diagnosed with a KIF1A gene mutation at the age of 2½. Patients diagnosed with severe KIF1A gene mutations may live only into ...
Scientists looking to provide relief for people with inflammatory bowel disease have turned to an unusual source for inspiration: barnacles. Inflammatory bowel disease (IBD), such as Crohn’s disease ...
Barbara Jacquelyn Sahakian receives funding from the Wellcome Trust. Her research work is conducted within the NIHR Cambridge Biomedical Research Centre (BRC) Mental Health and Neurodegeneration ...
This past spring, a biotech company announced the first use of a new gene-editing technology in people to fix an errant gene that causes a severe immune disorder. In June, a baby born with a ...
IgG4-related disease (IgG4-RD) is a chronic inflammatory condition. To treat it, doctors often prescribe corticosteroids to reduce inflammation and lower IgG4 levels. But long-term corticosteroid use ...
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