The prevalence of PBC is expected to rise in the United States and the wider world, requiring concrete, proactive action.

The results of the current meta-analysis reinforce the safety and efficacy of marstacimab in reducing annualized bleeding rates among patients with severe hemophilia A and B.

The appendicular lean mass was lower in patients with Fabry disease at a mean of 20,324 g compared to 25,529 g in healthy people.

The updated 2025 BSR management recommendations for patients with AAV provide systematic and evidence-based recommendations to support UK clinicians in managing AAV across the entire life course.

A CRISPR/Cas9-modified Janus kinse 2 V617F model may be useful to develop new therapies against myeloproliferative neoplasms.

Cyclophosphamide prophylaxis for graft versus host disease after allogeneic hematopoietic stem cell transplantation in MF is very effective.

Researchers sought to characterize RBC and platelet transfusion practices and found significant variability in neonatal blood transfusion practices.

Bilirubin results may differ between neonates of different ethnicities, a possibility that should inform the interpretation of these results.

Concurrent systemic mastocytosis (SM) negatively impacted the prognosis of acute myeloid leukemia (AML) with RUNX1::RUNX1T1 fusion.

A case has been reported of successful sedation anesthesia for gastroscopy in a patient with cold agglutinin disease (CAD).

Treatment with tafamidis over a 1-year period stabilized several cardiac biomarkers in patients with ATTR-CM, a study found.

Researchers presented the case of a patient with CIDP who experienced syncope and new-onset bifascicular block while being treated with IVIG.