Sanofi's venglustat accepted for priority review in the US to treat type 3 Gaucher disease Paris, May 28, 2026. The US Food and Drug Administration (FDA) has granted priority review to the new drug ...

MDS-UPDRS scores remained stable and durable across overall study population after 150 days of treatment with ...

The US Food and Drug Administration (FDA) has granted priority review to the new drug application (NDA) for Sanofi’s (Euronext: SAN) venglustat, a novel, investigational oral glucosylceramide synthase ...

Kyle Busch’s family says the NASCAR superstar died after severe pneumonia progressed into sepsis, a dangerous condition that ...

Keaton Herzer tells PEOPLE a newer targeted therapy unexpectedly shrank his tumors enough to qualify for a liver transplant ...

People with a rare genetic disorder that damages the amygdala are helping neuroscientists rethink how the brain shapes fear, ...

May is ALS Awareness Month, and a Chicago couple is tackling the devastating disease head-on.

Lucia Adarve had a long list of symptoms that no one could diagnose. Her mother Lisa was determined to find an answer.

Actress Erin Moriarty is speaking candidly about the difficult health journey that eventually led to a Graves’ disease ...

Live Science spoke with Alika Maunakea, an Native Hawaiian epigeneticist, about how epigenetics underpins health disparities ...

Celebrities including Russell Andrews and Eric Dane have fought ALS while inspiring others and advocating for research ...